Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders
Park Julien , Bremova-Ertl Tatiana , Brands Marion , Foltan Tomas , Gautschi Matthias , Gissen Paul , Hahn Andreas , Jones Simon , Arash-Kaps Laila , Kolnikova Miriam , Patterson Marc , Perlman Susan , Ramaswami Uma , Reichmannová Stella , Rohrbach Marianne , Schneider A. Susanne , Shaikh Aasef , Sivananthan Siyamini , Synofzik Matthis , Walterfarng Mark , Wibawa Pierre , Martakis Kyriakos , Manto Mario
Forschungsartikel (Zeitschrift) | Peer reviewedDetails zur Publikation
Fachzeitschrift: Journal of Neurology (J Neurol)
Jahrgang / Bandnr. / Volume: 271
Ausgabe / Heftnr. / Issue: 10
Status: Veröffentlicht
Veröffentlichungsjahr: 2024
Stichwörter: Clinical outcome assessments; Lysosomal storage disorders; Scale for the assessment and rating of ataxia
Autor*innen der Universität Münster